Boys Treated With Gene Therapy for Rare Brain Disease Doing Well 6 Years Later
THURSDAY, Oct.10, 2024 (HealthDay News) — Most boys treated with breakthrough gene therapy for a rare but deadly brain illness are faring well six years later, two new reports find. The 77 boys were treated for cerebral adrenoleukodystrophy (CALD), a formerly incurable and progressive genetic brain disease that typically ledContinue Reading